Patient Community
Understanding patients’ needs to further develop therapies | 7/27/2020
When developing a treatment for a disease, it is easy to lose sight of the most important part of the equation: the patient. What makes uniQure special is that we place patients at the center of every discussion.uniQure is committed to the patient community through our medicine, biotechnology, and patient advocacy activities. We believe that the patient voice, together with our expertise and technologies, will inform the horizon for new …
Health Care Roundtable | 7/27/2020
… We were monitoring the news from China in early January as the first airlifts began arriving in the U.S. When the lockdown began in March, we had already begun communications educating our staff and patient community about the coronavirus. When we shutdown elective procedures we knew we would have a significant financial impact but we also knew it was all hands-on deck to address COVID-19 because we were …
StuffThatWorks Raises $9M in Seed Funding | 7/25/2020
StuffThatWorks , a Tel Aviv, Israel-based patient community platform, raised $9M in seed funding. Backers included Bessemer Venture Partners, 83North, and Ofek Ventures. Founded by Yael Elish, Ron Held, and Yossi Synett, StuffThatWorks provides a patient community platform that harnesses crowdsourcing and AI technology to empower people to share their experiences in an organized way to discover which treatments work best and for whom. Initially, no immediate information is available …
… variation of applications to interface predictably with mobile devices, cell phones and computer systems to support the community so patients could easily connect. That has been a huge success and I don’t see the patient community wanting to go back to normal because virtual care is so convenient.” In partnership with the health system’s governance group, Mr. Brown set priorities to re-rationalize the next 12 months and then cascade …
Putting patients at the centre of COVID-19 research | 7/24/2020
… as official supporters. Our website has received 189,000 views from users in 163 countries. Patient engagement Four days after declaring the pandemic, the WHO released a plan recommending key strategies for engaging with the patient community . In those guidelines, the WHO makes it clear that patients provide an important perspective on the health-care system because they can assess the quality of care and the barriers to access. Patients are …
Study finds interest in online dietary support among adults with kidney failure | 7/24/2020
Adults who receive maintenance hemodialysis 2 or more times per week expressed interest in an online patient community that includes access to a registered dietitian, according to survey results. “Technology and social media have promise for helping patients with [end-stage renal disease] ESRD adhere to their prescribed diets,” Claudia Mejia, MS, CLC, of the department of allied health sciences at the University of Connecticut, and colleagues wrote. “Two-thirds …
The idea that most men will recover meaningful erectile and sexual function after treatment for prostate cancer has long been disputed by many in the patient community . We now seem to have some better data supporting the patient perspective. According to a presentation by Deschamps at the European Association of Urology 2020 virtual congress, reported on by Renal and Urology News , the so-called EUPROMS study, which surveyed nearly 3,000 …
… for possessing the key qualities that make our company both human and successful. Leadership at Verisys is all about ethical and transparent accountability for our key constituents, our team members, customers, investors, and the patient community .” Infusing Verisys’ mission of protecting health care consumers by enforcing provider competency to assure patient safety and quality care inspires the entire organization towards excellence and job satisfaction. “Leadership is part of each and …
by [email protected] StuffThatWorks Raises $9M Seed Round to Empower People with Health Conditions to Discover Which Treatments Work Best TEL AVIV, Israel , July 23, 2020 /PRNewswire/ — StuffThatWorks, the patient community platform that harnesses crowdsourcing and AI technology to empower people to share their experiences in an organized way to discover which treatments work best and for whom, launched today backed by $9 Million in seed funding from Bessemer Venture …
‘Next remdesivir’ should cost below $1,000: patient poll | 7/23/2020
… more leadership in their treatment journey,” noted Jack Barrette, CEO of Wego Health. “The industry has a tremendous opportunity to step in and harness the voices of patients living with chronic illnesses to build patient community trust and establish support.” One of those areas is in setting price. Had Gilead tapped the opinion of the patient community and disclosed as such in its messaging, both remdesivir’s price and the market …
Life of a Clinical Geneticist: Dealing Often With Heartless Bureaucracy | 7/23/2020
… personal opinions only. Following is a summary of my discussion with Tom. While the value of genetic testing is indisputable and accepted throughout the clinical genetics community, and more and more understood by the patient community , getting testing approved by insurance is now the biggest hurdle a clinician is facing these days. Our discussion focused on the challenges clinical geneticists encounter when working through the process of getting a genetic …
Should I Check Into Rehab During COVID-19? | 7/23/2020
… House which is part of our four acre campus. We currently give every detox patient their own room because our campus is large enough to make that accommodation. They are separated from our general patient community who are in ongoing residential care. Because patients brand new to recovery would check into detox initially anyway, patients do not experience much of a difference staying in this house for “quarantine”. Their goal …
… Center for Heart Valve Disease at Northwestern Medicine and the clinical study’s principal investigator. “Our work with Eko aspires to extend the auscultatory expertise of cardiologists to more general practitioners to better serve our patient community , playing a pivotal role in growing the future of cardiovascular medicine.” Eko and Northwestern first announced their collaboration in March 2019 to provide a simpler, lower-cost way for clinicians to identify patients with …
Global Summit On Kidney Disease Innovation And Choice Engages 70 Countries | PR Newswire | 7/22/2020
… kidney patients worldwide to elevate patient insights among an international network of researchers, clinical trial experts, innovators, companies, and government leaders. This ground-breaking announcement is the first of its kind in the kidney patient community and signals widening support for an International Kidney Consortium . All 2020 Global Summit presentations are now available OnDemand and will continue to reach tens of thousands of additional viewers across the world to increase …
… first large pivotal trial in MSA, and we all look forward to the results by the end of next year.” Philip M. Fortier, MA, Executive Director of the Defeat MSA Alliance, commented, “The MSA patient community is optimistic that the M-STAR study will figure prominently in the history of our collective efforts to defeat this debilitating disease. On behalf of MSA patients worldwide, we are thankful to Biohaven for …
… to earlier lines of therapy,” said Gisela Schwab, M.D., President, Product Development and Medical Affairs and Chief Medical Officer, Exelixis. “More data are needed to better understand the sequential use of treatments for this patient community , and we look forward to learning more about the potential role of the combination of cabozantinib and atezolizumab following checkpoint inhibitor therapy in this pivotal trial with our partner Roche.” CONTACT-03 is a …
… to earlier lines of therapy,” said Gisela Schwab, M.D., President, Product Development and Medical Affairs and Chief Medical Officer, Exelixis. “More data are needed to better understand the sequential use of treatments for this patient community , and we look forward to learning more about the potential role of the combination of cabozantinib and atezolizumab following checkpoint inhibitor therapy in this pivotal trial with our partner Roche.” CONTACT-03 is a …
External Resources and Information Related to Patients’ Experience | 7/20/2020
Print This webpage is intended to facilitate public discussion of patient-focused drug development and evaluation. This webpage provides links to certain publicly available external reports and resources relating to patient experience data. The patient community , patient advocates, researchers, drug developers, and federal agencies may find these materials useful. Please note that although FDA reviews the materials at these links before posting them to ensure that the materials are within …
… Immunodeficiency patient and physician community… More than 33 years after its creation, the Jeffrey Modell Foundation continues its mission of hope, advocacy, and action by vigorously supporting physicians, researchers, and the ever-expanding global patient community - directing its efforts toward early diagnosis, meaningful treatments, equal access to care, and, ultimately, cures for Primary Immunodeficiency. To learn more about the Modells and the Jeffrey Modell Foundation please visit: www.info4pi.org Thank you …
… with the NLRP3 inflammasome since our foundation. Activation of NLRP3 is implicated in a very wide spectrum of diseases, of which CAPS is just one. Today’s news is a positive development for the CAPS patient community , for whom there are currently limited treatment options. We look forward to further developing Inzomelid and initiating our Phase II study in CAPS later this year.” About Inflazome Inflazome is a biotech company leading …
… negative and HER2-dependent. “The LeadAction Breast Cancer du Sein Competition is unique and innovative! It is translated by the convergence of three vital scientific and social innovation components, namely science, industry and the patient community . Therefore, by jointly launching this call, IRICoR and the Quebec Breast Cancer Foundation have met the glaring needs of the people affected by breast cancer, by supporting large-scale projects that will result in …
… North America . “Kyowa Kirin is seeking to sponsor work that can have a profound patient impact. We hope this grant program will encourage researchers and organizations with an interest in helping the African-American patient community improve outcomes.” Kyowa Kirin encourages proposals from the following individuals or organizations who are focused on a mission related to patient education and/or healthcare improvement: Patient advocacy organizations or non-profit foundations; organizations …
… who need them most. NORD is made strong together with over 300 disease-specific member organizations and their communities and collaborates with many other organizations on specific causes of importance to the rare disease patient community . Visit rarediseases.org About PlatformQ Health PlatformQ Health Education is the leading provider of interactive digital medical education for clinicians, patients and caregivers. To improve patient care, PlatformQ Health Education creates video-first educational modules …
… with a cane. I became compelled to educate and heighten awareness for the local patient communities and felt a passion and determination to open a cannabis-focused education wellness center to help educate the patient community ’s need for the pain, anxiety and sleeplessness coupled with various diseases like Cancer, MS and Parkinson’s ect. WB: Please tell me about your company? What are your six and twelve month goals? VV: Synchronicity …
… on Advisory Committee panels for rare disease drugs. Each year, the FDA must prepare a report showing how many rare disease drug applications were reviewed by each division at the Agency. Members of the patient community must be consulted when devising or reviewing a Risk Evaluation and Mitigation Strategy (REMS) for a rare disease drug that calls for patient participation. The General Accounting Office must review the EU process for …
COVID-19
… based Piedmont Healthcare operated in a 90-day crisis management mode, which required all team members to focus on their COVID-19 response. For the IT team, that meant supporting a steep influx in virtual … has been a huge success and I don’t see the patient community wanting to go back to normal because virtual care is so convenient.” In partnership with the health system’s governance group, Mr. Brown set …
NIH
Global Summit On Kidney Disease Innovation And Choice Engages 70 Countries | PR Newswire | 7/22/2020
… and Kidney Diseases (NIDDK) and Chief of the Molecular and Clinical Hematology Branch at the U.S. National Institutes of Health (NIH). Dr. Rodgers is an international voice for patient inclusion in research and innovation, a … announcement is the first of its kind in the kidney patient community and signals widening support for an International Kidney Consortium . All 2020 Global Summit presentations are now available OnDemand and will continue to reach …
National Institutes of Health
Global Summit On Kidney Disease Innovation And Choice Engages 70 Countries | PR Newswire | 7/22/2020
… of Diabetes and Digestive and Kidney Diseases (NIDDK) and Chief of the Molecular and Clinical Hematology Branch at the U.S. National Institutes of Health (NIH). Dr. Rodgers is an international voice for patient inclusion in … announcement is the first of its kind in the kidney patient community and signals widening support for an International Kidney Consortium . All 2020 Global Summit presentations are now available OnDemand and will continue to reach …
Food and Drug Administration
… MSA and amyotrophic lateral sclerosis (ALS). Verdiperstat has received Orphan Drug and Fast Track designations for MSA from the U.S. Food and Drug Administration (FDA), as well as Orphan Drug designation from the European Medicines … Executive Director of the Defeat MSA Alliance, commented, “The MSA patient community is optimistic that the M-STAR study will figure prominently in the history of our collective efforts to defeat this debilitating disease. On …
Patient-Centered Research
UPPER NYACK, N.Y.–(BUSINESS WIRE)–Apr 22, 2020– Today the Global Healthy Living Foundation (GHLF) and CreakyJoints ®, its digital patient community for people with all forms of arthritis, announced the launch of the Autoimmune COVID … 19,” said study lead Shilpa Venkatachalam, PhD., Associate Director of Patient-Centered Research at CreakyJoints and co-principal investigator of ArthritisPower. “We need information about the impact of COVID-19 on patients with autoimmune, rheumatic …
Biotech
… a $15,000 grant award from the Russel Hill Cancer Foundation. The award will support a collaborative project with HudsonAlpha Associate Biotech iXpressGenes, Inc. aimed at accelerating PHTS Research. “Currently, there is no cure for our … 501C3 organization founded in December 2013 to support the PHTS patient community through programs and patient assistance, research initiatives, and education. The Russell Hill Cancer Foundation of Huntsville, Alabama is a 501C3 organization committed to …
Medicare
… patient community and will continue to do what we can to ensure our patients and healthcare professionals are supported during these challenging times.” The VALCHLOR copay program is only available for US and Puerto Rico residents who are 18 or older and have commercial health insurance. Patients ineligible for the VALCHLOR copay/coinsurance program include those enrolled in Medicare, Medicaid, VA/DoD (Tricare), the Indian Health Service, or any other …
CDC
… its operations. The Company has taken steps in line with guidance from the U.S. Centers for Disease Control and Prevention (CDC) and the State of California to protect the health and safety of its employees … working closely with its clinical sites, physician partners and the patient community to monitor the potential impact of the evolving COVID-19 pandemic. The Company remains committed to its clinical programs and development plans, but …
Department of Health and Human Services
… a member enrollment portal and claims processing system for a national payer, a federal adverse event reporting portal for the Department of Health and Human Services, a fraud prevention system that processes over six million … organizations on specific causes of importance to the rare disease patient community. Visit rarediseases.org . SOURCE National Organization for Rare Disorders (NORD) Related Links https://rarediseases.org …
Medical Education
… to treatment, particularly with IVIG, so the next program focuses on those themes,” explained Dr. Anne Roc, Vice President of Medical Education at PlatformQ Health. “With so much ground to cover on this rare neurologic … research funding and advocacy for legislation that directly affects our patient community. We are working toward a future where patients coping with this rare set of neurologic conditions do not suffer alone and that every …
Mental Health
Podcast | Chronic Illness and Depression | 12/2/2019
… Zimmerman also started to experience depression. Unable to tackle both, Jackie chose to focus on her physical health, letting her mental health deteriorate quickly — and dangerously. In this episode, we discuss the mind-body connection … as an authority on chronic illness, patient-centric healthcare, and patient community building. She lives with multiple sclerosis, ulcerative colitis, and depression. You can find her online at JackieZimmerman.co , Twitter , Facebook , and LinkedIn. Computer Generated …
Diagnostic Tests
IFFGD Shares GI Developments with #GivingTuesday | PR Newswire | 12/2/2019
… conducted at medical meetings with GI healthcare experts who highlight research and developments in the GI field, as well as, share valuable insights to raise awareness about research and inform the general and patient community affected by a chronic gastrointestinal disorder. The videos are available on IFFGD’s YouTube channel. In 2020, IFFGD wants to continue the GI Research on the Road program with a goal of 40 new videos from …
Regenerative Medicine
Remarks by Anna Abram to the Biocom Celebration of Life Dinner - 11/21/2019 | 11/22/2019
… to medical product development for rare diseases; and most recently, we created the Patient Engagement Collaborative, a forum for the patient community and regulators to discuss increasing patient engagement in medical product development and regulatory … created a priority review pathway for breakthrough medical devices, the regenerative medicine advanced therapy designation program, and a limited population approval pathway for antibacterial and antifungal drugs, among other things. It also established a clear …
Patient Engagement
Remarks by Anna Abram to the Biocom Celebration of Life Dinner - 11/21/2019 | 11/22/2019
… at various ways to enhance how to incorporate the patient experience into FDA’s regulatory discussions. In this patient-focused paradigm, patient engagement is increasing, including relying more on patients themselves as a rich source of … we created the Patient Engagement Collaborative, a forum for the patient community and regulators to discuss increasing patient engagement in medical product development and regulatory discussions at FDA. Concurrent with this greater focus on leveraging …
Gene Therapy
Remarks by Anna Abram to the Biocom Celebration of Life Dinner - 11/21/2019 | 11/22/2019
… therapies, selecting the right treatment for the right patient, resulting in the advancement of immunotherapy and the first FDA-approved gene therapy products. And now we’re grappling with how regulators should address the so-called … we created the Patient Engagement Collaborative, a forum for the patient community and regulators to discuss increasing patient engagement in medical product development and regulatory discussions at FDA. Concurrent with this greater focus on leveraging …
Clinical Data
… all members of the community to register for this meeting in person or online here . “We’re honored to bring this patient community together in collaboration with AMDA and UPF, and to have leaders from the … diseases. MDA’s Neuromuscular ObserVational Research (MOVR) data hub gathers longitudinal clinical data for multiple neuromuscular diseases to improve health outcomes and accelerate therapy development. MDA supports the largest network of multidisciplinary clinics providing best in …
Patient Recruitment
StudyKIK Introduces its New Clinical Trial Patient Recruitment Call Center Technology Platform, Increasing its Pre-screen Volume to Over 4,000 Patients Daily Share Article The newest custom technology update to StudyKIK’s in-house Patient Qualification Department will allow StudyKIK to provide wider pre-screening support to research site partners, increasing clinical trial feasibility. These improvements have increased our agents’ efficiency by 90% and improved the quality of our pre-screening …
Precision Medicine
SOUTH SAN FRANCISCO, Calif. , Nov. 20, IDEAYA Biosciences, Inc. (Nasdaq: IDYA ), an oncology-focused precision medicine company committed to the discovery and development of targeted therapeutics to treat cancer, announced it has presented data from … continued collaboration with our clinical investigators, the FDA and the patient community,” said Yujiro S. Hata , Chief Executive Officer and President at IDEAYA Biosciences. About IDEAYA Biosciences IDEAYA is an oncology-focused precision medicine company …
Hospital Management
… hospital management in stopping child abductions and child-swaps, besides tracking and securing hospital assets. It brings more awareness and alertness among the staff and the healthcare professionals through real-time alerts to quickly respond to child theft and other breaches. The initiative is to scale and leverage County Manukau District Health Board’s commitment to ensuring security and on-time services to its patient community. Addressing to the needs, WiSilica …
RTLS
… time alerts to quickly respond to child theft and other breaches. The initiative is to scale and leverage County Manukau District Health Board’s commitment to ensuring security and on-time services to its patient community. Addressing to the needs, WiSilica, in collaboration with CMS, deployed wearable tags and asset tags that track infants and hospital devices in real-time. Being a comprehensive tracking and alerting system, the tags send instant …
Patient Safety
… patient community and drive greater efficiency for the organization. The Center of Excellence program recognizes world-class health systems that utilize Sunquest solutions to support the strategic direction of their organization. This includes establishing and promoting best practices that improve patient safety, decrease the cost of healthcare, streamline provider care, and provide thought leadership and recommendations on new and existing Sunquest products. The Sunquest Center of Excellence program identifies those …
EMR
UPPER NYACK, N.Y.- CreakyJoints® , a Global Healthy Living Foundation patient community, will present five posters, some in partnership with major academic institutions, at the 2019 ACR/ARP Annual Meeting in Atlanta, GA (Nov. 8-12, 2019 … 435) Comparison of Medication New User Definitions in Multi-Specialty EMR Data (Abstract: 2067) Art for Arthritis: A New Approach (Abstract: PP06) About ArthritisPower® Created by CreakyJoints ® and supported by a multiyear, multimillion dollar investment …
Electronic Medical Record
… study design limited the generalisability of the results. The data on readmission might be inaccurate due to the use of electronic medical records to acquire the data. Introduction Inappropriate prescribing, which encompasses potentially inappropriate medications … results of this research to study participants or the relevant patient community. Results The baseline characteristics of the 739 elderly hospitalised patients are shown in table 1 . Of those, the median patient age was 82 …
Patient Satisfaction
… All Intalere members, both acute and non-acute care, may submit projects that were completed within this past year in the areas of financial and operational improvements, quality and patient care delivery and patient satisfaction, supply chain and data management, and community impact and innovation. Entry forms must be received by Intalere no later than January 31, 2020. Entries will be reviewed by a panel of judges and winners will …
Clinical Research
… I’m very proud to highlight that we were recently honored with our third consecutive Eagle Award from the Society for Clinical Research Sites. The Eagle Award recognizes the CRO that best exemplifies a site-focused … engaged trial participants. We believe that engaging them as a patient community through our catalyst site partners using our commercial communications and social listening capabilities allows us to leverage behavioral insights to design new ways …
PlatformQ Health
NORD taps PlatformQ Health to Transition Living Rare, Living Stronger Patient and Family Forum to Comprehensive, Interactive Virtual Event Share Article Rare disease conference to be held online, featuring dedicated tracks patients and families and … organizations on specific causes of importance to the rare disease patient community. Visit rarediseases.org About PlatformQ Health PlatformQ Health Education is the leading provider of interactive digital medical education for clinicians, patients and caregivers. To …
AbbVie
… the U.S. News provided by Jun 23, 2020, 07:30 ET Share this article NORTH CHICAGO, Ill. , June 23, 2020 /PRNewswire/ – AbbVie (NYSE: ABBV ), a research-based global biopharmaceutical company, today announced that the U.S. Food … option for WM patients and our commitment to supporting this patient community.” WM typically affects older adults and is primarily found in the bone marrow, although lymph nodes and the spleen may also be affected …
WEGO Health
WEGO Health Launches Pharmaceutical Grade Influencer Marketing℠ | PRWeb | 6/17/2020
WEGO Health Launches Pharmaceutical Grade Influencer Marketing℠ Share Article Trust versus results. Why should brands have to choose? BOSTON WEGO Health, a mission-driven patient collaboration company, launched today the only influencer marketing program designed … create content crafted to meet the authentic needs of the patient community as well as pharma business and regulatory requirements,” says WEGO Health Chief Client Officer, Kristen Hartman. “But the real excitement is in how …
PatientsLikeMe
… PatientsLikeMe , an online patient community portal, with the intent of folding the startup into its healthcare innovation research arm. Interestingly, AbleTo has also been on the purchasing side of an M&A within the last year, as it had acquired a fellow virtual behavioral health company named Joyable in March 2019. Tags …
Johnson & Johnson
4 Ways to Help Nurses During the Coronavirus Pandemic | PR Newswire | 4/20/2020
… Support Fund The American Nurses Foundation’s Coronavirus Response Fund for Nurses is a nationwide effort to provide direct financial assistance, mental health support and science- and data-based resources to benefit nurses. The Johnson & Johnson company and its TYLENOL brand made a $1.5 million commitment to launch this fund. A portion of the donations will help support Nurses House, Inc. , a national fund for registered nurses in need. The American …
Protalix
CARMIEL, Israel , March 18, Protalix BioTherapeutics, Inc. (NYSE American: PLX) (TASE: PLX), a biopharmaceutical company focused on the development, production and commercialization of recombinant therapeutic proteins produced by its proprietary ProCellEx ® plant cell-based protein … Protalix’s commitment to bring important treatment options to the Fabry patient community,” said Dror Bashan , Protalix’s President and Chief Executive Officer. “This funding gives us the runway and ability to complete our pivotal Phase III …
Sanofi Genzyme
Area Business Manager Dupixent - Tampa - Tampa, FL, , USA #jobs #Tampa pls RT | 11/27/2019
… Sanofi Genzyme focuses on developing specialty treatments for debilitating diseases that are often difficult to diagnose and treat, providing hope to patients and their families. Sanofi Genzyme has pioneered the development and delivery of transformative therapies for patients affected by rare and debilitating diseases for over 30 years. We accomplish our goals through world-class research, collaboration with the global patient community, and with the compassion and commitment of our …
Genzyme
Area Business Manager Dupixent - Tampa - Tampa, FL, , USA #jobs #Tampa pls RT | 11/27/2019
… Genzyme focuses on developing specialty treatments for debilitating diseases that are often difficult to diagnose and treat, providing hope to patients and their families. Sanofi Genzyme has pioneered the development and delivery of transformative therapies for patients affected by rare and debilitating diseases for over 30 years. We accomplish our goals through world-class research, collaboration with the global patient community, and with the compassion and commitment of our employees …
Genentech
Associate Director - Alliance and Advocacy Relations : South San Francisco | 11/26/2019
… Genentech representative to external advocates, establish and maintain in-depth knowledge of Genentech business plans, and engage relevant advocates to best support the patient community and Genentech’s priorities. This individual will be a member of Genentech’s BioOncology AAR team and will report to the Director for BioOncology-AAR. This position location is flexible and can be based either in Genentech’s South San Francisco headquarters or the Washington D.C. office. Sample …
Pfizer
… Executive Officer. “We are committed to the completion of this program with positive results for the benefit of the Fabry patient community.” The Company and Chiesi also announced that they have reached an agreement with … the regulatory authorities of other countries. Protalix has licensed to Pfizer Inc. the worldwide development and commercialization rights for taliglucerase alfa, excluding Brazil , where Protalix retains full rights. Protalix’s development pipeline includes the following product …
Amgen
UPPER NYACK, N.Y.- CreakyJoints® , a Global Healthy Living Foundation patient community, will present five posters, some in partnership with major academic institutions, at the 2019 ACR/ARP Annual Meeting in Atlanta, GA (Nov. 8-12, 2019 … impossible without MTX. This study was conducted with support from Amgen Inc and with GHLF research funds. Which symptoms are most important to arthritis patients in their experience and tracking of disease activity and treatment …
Novartis
… prefer that I speak more often more publicly on this issue, and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this … Spinraza sites treating SMA. Based on the very strong results Novartis demonstrated with their recent launches of Zolgensma and understanding the label and the differences in patient population sizes between the two disease states, we …
Sarepta Therapeutics
Sarepta Therapeutics, Inc. (NASDAQ: SRPT ) Q3 2019 Earnings Conference Call November 7, 2019 4:30 PM ET Company Participants Ian Estepan - Senior Vice President, Chief of Staff and Corporate Affairs Douglas Ingram - President and Chief Executive … issue, and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this therapy a lot faster. I have no intention of doing …
Eli Lilly
… record of raising capital and growing companies, as well as a deep understanding of the cystic fibrosis and rare disease patient community we are focused on. We look forward to their contributions.” Dr. Alexey Margolin … and CEO until 2010, when the company was acquired by Eli Lilly. As Chief Scientific Officer for Altus Pharmaceuticals, he helped build a portfolio of products for rare diseases. Dr. Margolin is the author of …
UnitedHealth
UnitedHealth’s contract battles with two large physician staffing agencies have notable implications for the industry amid the ongoing debate over ways to mitigate surprise medical bills, a new analysis shows. Moody’s Investors Service released a … bills that harm a hospital’s reputation and relationship with the patient community, according to the report. “If the profitability of the physician staffing sector experiences material long-term weakness, the ultimate financial pinch could be …
Ultragenyx
September 03, 2019 08:30 ET Source: Ultragenyx Pharmaceutical Inc.; GeneTx Biotherapeutics LLC SARASOTA, Fla. and NOVATO, Calif., Sept. 03, 2019 (GLOBE NEWSWIRE) – GeneTx Biotherapeutics LLC and Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused … GeneTx, a company launched because of the efforts of this patient community, is the first in this space to receive the Rare Pediatric Disease Designation.” GTX-102 is currently in late preclinical development, and an …
Quintiles
… million patients in Colombia are elderly and suffer from chronic pain, anxiety, depression or are in palliative care (Source: IMS quintiles) Khiron medical product pipeline focused on priority conditions associated with aging, including chronic pain … market as part of our strategy to focus on the patient community in Latin America . This relationship with CAGG increases our ability to deepen interactions with health professionals in the field and to educate on …
Nurx
Nurx Receives $52 Million For Expanding Access To Sensitive Health Needs | 8/26/2019
Nurx, a health tech company that is providing convenient and affordable care for sensitive needs, announced it raised $52 million Nurx — the health tech company providing convenient and affordable care for sensitive health needs — announced … services for sensitive health needs as well as grow its patient community to reach more people who face systemic barriers to healthcare. And Nurx will also focus on expanding its medical provider team as well …
GSK
… patients and their families living with lupus, a chronic, inflammatory, autoimmune disease that affects approximately five million people globally. 1,2 GSK conceived, developed and led the ‘ A Vision for Lupus ’ initiative in collaboration with a … report will help raise the global voice of the lupus patient community and drive a much-needed change to improve the lives of patients living with lupus.” Notes to editors About Systemic Lupus Erythematosus (SLE …
Merrill Lynch
… Whitney Ijem - Guggenheim Christopher Marai - Nomura Brian Abrahams - RBC Capital Markets Debjit Chattopadhyay - H.C. Wainwright Tazeen Ahmad - Bank of America Merrill Lynch Gena Wang - Barclays Salveen Richter - Goldman Sachs Danielle Brill - Piper Jaffray Joel Beatty … issue, and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this therapy a lot faster. I have no intention of doing …
… Doug Treco, Ph.D., President and Chief Executive Officer of Ra Pharmaceuticals commented: “UCB shares our commitment to the rare disease patient community and our goal of developing novel, accessible, and cost-effective therapies in the … and underwritten by BNP Paribas Fortis and Bank of America Merrill Lynch. Pro-forma for this acquisition, UCB’s new net debt / rEBITDA ratio would be in the range between 1.5 and 2.0 times with rapid …
SVB Leerink
… prefer that I speak more often more publicly on this issue, and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this … year. Operator Our next question comes from Joseph Schwartz of SVB Leerink. Your line is open. Unidentified Analyst Hi, good evening. Thanks for taking my questions. This is Dae Gon [ph] dialing in for Joe …
Sarepta Therapeutics (SRPT) Q3 2019 Earnings Call Transcript | The Motley Fool | 11/8/2019
… that I speak more often and more publicly on this issue and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this … year. Operator Our next question comes from Joseph Schwartz of SVB Leerink. Your line is open. Dae Gon – SVB Leerink – Analyst Hi, good evening. Thanks for taking the question. This is Dae Gon dialing in …
Piper Jaffray
… Debjit Chattopadhyay - H.C. Wainwright Tazeen Ahmad - Bank of America Merrill Lynch Gena Wang - Barclays Salveen Richter - Goldman Sachs Danielle Brill - Piper Jaffray Joel Beatty - Citi Ritu Baral - Cowen Brian Skorney - Robert W. Baird Liisa Bayko … issue, and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this therapy a lot faster. I have no intention of doing …
… Medical Officer Conference Call Participants Joshua Schimmer - Evercore ISI Marc Goodman - SVB Leerink Timothy Lugo - William Blair & Company David Amsellem - Piper Jaffray Companies Stacy Ku - Cowen and Company Irina Koffler - Mizuho Securities Tian Sun - Needham … I was just curious if the feedback from the physician, patient community has been that this is more helpful, this is easy, it’s working. Is there anything in the marketing messaging or the focus of …
Goldman Sachs
… Abrahams - RBC Capital Markets Debjit Chattopadhyay - H.C. Wainwright Tazeen Ahmad - Bank of America Merrill Lynch Gena Wang - Barclays Salveen Richter - Goldman Sachs Danielle Brill - Piper Jaffray Joel Beatty - Citi Ritu Baral - Cowen Brian Skorney - Robert … issue, and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this therapy a lot faster. I have no intention of doing …
Sarepta Therapeutics (SRPT) Q3 2019 Earnings Call Transcript | The Motley Fool | 11/8/2019
… that I speak more often and more publicly on this issue and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this … mark. Operator Our next question comes from Salveen Richter of Goldman Sachs. Your line is open. Salveen Richter – Goldman Sachs – Analyst Good afternoon. Thanks for taking my question. So with regard to the gene therapy …
William Blair
… prefer that I speak more often more publicly on this issue, and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this … afterwards. Operator Our next question comes from Tim Lugo of William Blair. Your line is open. Unidentified Analyst Hi, this is John on for Tim. Thanks for the question. I was just wondering if you …
Sarepta Therapeutics (SRPT) Q3 2019 Earnings Call Transcript | The Motley Fool | 11/8/2019
… that I speak more often and more publicly on this issue and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this … afterwards. Operator Our next question comes from Tim Lugo of William Blair. Your line is open. John Boyle – William Blair – Analyst Hi. This is John on for Tim. Thanks for the question. I was just …
Centerview Partners
… Doug Treco, Ph.D., President and Chief Executive Officer of Ra Pharmaceuticals commented: “UCB shares our commitment to the rare disease patient community and our goal of developing novel, accessible, and cost-effective therapies in the … is acting as legal advisor to UCB on this transaction. Centerview Partners is acting as exclusive financial advisor to Ra Pharma on this transaction. Latham & Watkins LLP is acting as legal advisor to Ra Pharma …
… Doug Treco, Ph.D., President and Chief Executive Officer of Ra Pharmaceuticals commented: “UCB shares our commitment to the rare disease patient community and our goal of developing novel, accessible, and cost-effective therapies in the … is acting as legal advisor to UCB on this transaction. Centerview Partners is acting as exclusive financial advisor to Ra Pharma on this transaction. Latham & Watkins LLP is acting as legal advisor to Ra Pharma …
Leerink Partners
… be very pleased and grateful for the high level of support and enthusiasm for this clinical program from the XLMTM patient community and the medical community. Turning to our second program, Crigler-Najjar is a … first. Operator Our next question comes from Joseph Schwartz with Leerink Partners. Joseph Schwartz I was wondering if you could talk a little bit about the variability in the measures that you’re collecting at baseline …
… our partnership’s continued progress and that we’re close to potentially delivering the first once-daily nebulized bronchodilator to the COPD patient community. I’ll now pass the call over to Renee to provide a financial update … Instructions] We’ll have our first question from Geoffrey Porges with Leerink Partners. Brad Canino Hi, this is Brad Canino on for Geoff. Thanks for taking the question. On the JAK, you plan to initiate a …
Mayo Clinic
… treatment for this devastating disease,” commented Dr. Phillip A. Low , M.D., Robert D. and Patricia E. Kern Professor of Neurology, Mayo Clinic, Rochester, MN. “I applaud the true champions of the M-STAR trial – the … Executive Director of the Defeat MSA Alliance, commented, “The MSA patient community is optimistic that the M-STAR study will figure prominently in the history of our collective efforts to defeat this debilitating disease. On …
… patient community faces in managing celiac disease and the experiences of clinical trial participants. In addition, Joseph A. Murray, MD of Mayo Clinic and leading researcher in the field of celiac disease, will discuss the roadblocks to research: Where we are now and what barriers remain on the path to actual therapies for celiac disease, including clinical trial update. Register online for a link to the webcast. The 2019 Beyond …
MD Anderson Cancer Center
… patient community,” said Dr. Srdan Verstovsek, MD, PhD, Professor in the Department of Leukemia at The University of Texas MD Anderson Cancer Center, Houston, Texas . “JAK inhibitors remain the cornerstone of myelofibrosis treatment but new options in this class are needed for the majority of patients who have difficulty tolerating the currently approved agents due to the cytopenias they can exacerbate or induce. Momelotinib could become a suitable alternative for …
… the MCRI Advisory Board selection committees. The founding members of the MCRI Scientific Advisory Board include: Robert Orlowski , MD, PhD, (MD Anderson Cancer Center), Ola Landgren , MD, PhD (Memorial Sloan Kettering Cancer Center), Guido Tricot … on Myeloma Crowd Radio to share their work with the patient community and answer patient questions. Both the Scientific and Patient Advisory Boards then selected two projects to fund. The final projects included CAR T …
The University of Texas MD Anderson Cancer Center
… patient community,” said Dr. Srdan Verstovsek , MD, PhD, Professor in the Department of Leukemia at The University of Texas MD Anderson Cancer Center, Houston, Texas . “JAK inhibitors remain the cornerstone of myelofibrosis treatment but new options in this class are needed for the majority of patients who have difficulty tolerating the currently approved agents due to the cytopenias they can exacerbate or induce. Momelotinib could become a suitable alternative for …
… patient community,” said Dr. Srdan Verstovsek, MD, PhD, Professor in the Department of Leukemia at The University of Texas MD Anderson Cancer Center, Houston, Texas . “JAK inhibitors remain the cornerstone of myelofibrosis treatment but new options in this class are needed for the majority of patients who have difficulty tolerating the currently approved agents due to the cytopenias they can exacerbate or induce. Momelotinib could become a suitable alternative for …
Dana Farber Cancer Institute
… the MMRF. “All of the work presented here at the International Myeloma Workshop reflects this focus and we’re proud to see the impact of our work with our world-class partners benefiting the patient community.” About the MMRF CoMMpass Study℠ The MMRF CoMMpass Study is a longitudinal study of patients with newly diagnosed active multiple myeloma. The goal is to map the genomic profile of each patient to clinical outcomes …
… Ola Landgren , MD, PhD (Memorial Sloan Kettering Cancer Center), Guido Tricot, MD, PhD ( University of Iowa ), Irene Ghobrial , MD, PhD (Dana Farber Cancer Institute), Rafael Fonseca , MD (Mayo Clinic Scottsdale), Noopur Raje , MD, PhD (Massachusetts … on Myeloma Crowd Radio to share their work with the patient community and answer patient questions. Both the Scientific and Patient Advisory Boards then selected two projects to fund. The final projects included CAR T …
Johns Hopkins University School of Medicine
… Anthony J. Filiano , Ph.D., Duke University ( Durham, NC ); Replacing brain enzymes with cells: Implications for malonic aciduria Michael Wolfgang , Ph.D., Johns Hopkins University School of Medicine ( Baltimore, MD ); Genetic and biochemical interaction of Mlycd and … organizations on specific causes of importance to the rare disease patient community. SOURCE National Organization for Rare Disorders (NORD) Related Links http://www.rarediseases.org …
… levels,” said Dr. Hilary Vernon , TAZPOWER trial investigator, Associate Professor of Pediatrics at the McKusick-Nathans Institute of Genetic Medicine, Johns Hopkins University School of Medicine and Director, Barth Syndrome Clinic at Kennedy Krieger Institute … 90%), physical activities (90%) and quality of life (80%). “Our patient community is in dire need of a therapy that addresses the complex, multi-system challenges that occur in Barth syndrome,” said Emily Milligan , Barth …
Peter L. Saltonstall
… GDPR, CCPA, PHI, PCI, and COPPA. “The technical team at NORD has vast experience, both in length and depth,” said Peter L. Saltonstall , President and CEO of NORD. “Under Prashant’s leadership we will light the … organizations on specific causes of importance to the rare disease patient community. Visit rarediseases.org . SOURCE National Organization for Rare Disorders (NORD) Related Links https://rarediseases.org …
Srdan Verstovsek
… patient community,” said Dr. Srdan Verstovsek , MD, PhD, Professor in the Department of Leukemia at The University of Texas MD Anderson Cancer Center, Houston, Texas . “JAK inhibitors remain the cornerstone of myelofibrosis treatment but new options in this class are needed for the majority of patients who have difficulty tolerating the currently approved agents due to the cytopenias they can exacerbate or induce. Momelotinib could become a suitable alternative for …
Seth Ginsberg
UPPER NYACK, N.Y.- CreakyJoints® , a Global Healthy Living Foundation patient community, will present five posters, some in partnership with major academic institutions, at the 2019 ACR/ARP Annual Meeting in Atlanta, GA (Nov. 8-12, 2019 … and their related information needs. CreakyJoints independently funded this study. Seth Ginsberg, president and co-founder of CreakyJoints added, “What’s important to emphasize is that while marijuana (and CBD) usage is growing among people with …
Doug Ingram
… www.sarepta.com and our 10-Q was filed with the SEC earlier this afternoon. Joining us on the call today are Doug Ingram, Sandy Mahatme, Bo Cumbo, Dr. Gilmore O’Neill and Dr. Rodino-Klapac. After our … issue, and/or that I would attempt to engage the patient community or others to assist, for instance, in applying external pressure to bring this therapy a lot faster. I have no intention of doing …
Dan Anglin
… with Canna Provisions Inc. for manufacturing and distribution of CannAmerica branded edibles products in the great State of Massachusetts ,” said Dan Anglin, CEO and Co-Founder of CannAmerica. “Having the opportunity to work in concert … and variety of products available to the Massachusetts medical cannabis patient community, that Canna Provisions, Inc. will manufacture and distribute CannAmerica branded products in Massachusetts , are forward-looking statements and contain forward-looking information. Generally …
Paula Martin
… Source: IMS quintiles) Khiron medical product pipeline focused on priority conditions associated with aging, including chronic pain management Khiron neurologist Paula Martinez to present keynote to more than 1,500 health professionals at Association congress in … market as part of our strategy to focus on the patient community in Latin America . This relationship with CAGG increases our ability to deepen interactions with health professionals in the field and to educate on …
Kevin Sullivan
… Kevin Sullivan , CEO of Appili Therapeutics . “Support from organizations like ACOA and the U.S. DOD demonstrates confidence in our ability to bring urgently needed anti-infectives to market. Our team is well positioned to realize the value in these opportunities, and to continue to fulfill our mission to become a global leader in infectious disease solutions that provide benefits for our patient community and value to our shareholders.” Financial Results …
Varsha Rao
Nurx Introduces Convenient & Private STI Home Test Kits | PR Newswire | 7/10/2019
… Varsha Rao . “We have built a significant amount of trust among our patient community for contraception and HIV prevention, and we’re committed to continue empowering our patients with the resources and knowledge on how to best protect themselves and their partners.” With Nurx’s STI Home Test Kits, there’s no need to find an available appointment, travel to the doctor’s office or clinic, or wait in line at the pharmacy. After …
Kathleen O'Donnell
ICYMI: ReWalk’s Restore technology for stroke patients featured in MD | PR Newswire | 11/30/2017
… assistive medical devices, and outlines the inspiration for a soft suit exoskeleton, with interviews with ReWalk CEO Larry Jasinski and Kathleen O’Donnell , lead of the medical exosuit program at Harvard’s Wyss Institute, ReWalk’s collaborative partner … is a soft suit exoskeleton designed for the stroke survivor patient community; exosuits are expected to offer additional use for other patient populations, including individuals with Parkinson’s Disease, Multiple Sclerosis or other mobility challenges where …
Brett Haumann
… patient community. While a significant number of COPD patients require or prefer nebulized therapy, these same patients currently have no access to a nebulized LAMA, broadly considered the cornerstone of COPD maintenance therapy,” said Brett Haumann , MD, Chief Medical Officer at Theravance Biopharma. “We are pleased with the comprehensive data package that was generated through our Phase 3 efficacy and safety studies and look forward to the FDA’s review of …
Robert Gottlander
OsteoReady LLC Announces New Management Structure | PR Newswire | 10/12/2017
… 2017 /PRNewswire/ – OsteoReady LLC, The Dental Implant Company for the General Practitioner ™ , announced a new management structure, effective today. Dr. Robert Gottlander , of New York, NY , has assumed the role of CEO of the Concord … with a basic surgical background and great access to the patient community. OsteoReady continues to develop its education platform, focus its training on efficient and safe techniques while developing products and solutions that are cost …
David Li
OsteoReady LLC Announces New Management Structure | PR Newswire | 10/12/2017
… CEO of the Concord, MA based company. Dr. Marc Nevins , of Boston, MA , was appointed Chairman of OsteoReady LLC. Dr. David Little , of San Antonio, TX , will continue his role as Clinical Director while Mike … with a basic surgical background and great access to the patient community. OsteoReady continues to develop its education platform, focus its training on efficient and safe techniques while developing products and solutions that are cost …
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